Diseases Treated by Hematopoietic Stem Cell Transplantation

Cancer (Oncology)

Leukemia

  • Acute myelogenous leukemia
  • Acute lymphoblastic leukemia
  • Chronic myelogenous leukemia
  • Juvenile myelomonocytic leukemia
  • Myelodysplastic syndrome

Lymphoma

  • Non-Hodgkin’s lymphoma
  • Hodgkin’s disease

Neuroblastoma

Solid Tumors

  • Wilm’s tumor
  • Brain tumor
  • Bone and soft tissue sarcoma
  • Germ cell tumor

Hematology

Bone marrow failure

  • Severe aplastic anemia
  • Congenital aplastic anemia
  • Fanconi anemia
  • Diamond Blackfan Anemia (DBA) 
  • Severe congenital neutropenia

Hemoglobinopathies

  • Thalassemia
  • Sickle cell disease
  • Paroxysmal nocturnal hemoglobinuria

Leukocyte disorders

  • Chronic granulomatous disease
  • Leukocyte adhesion deficiency
  • Chediak Higashi syndrome

Immunological Disorders

  • Severe combined immune deficiency
  • ADA deficiency
  • Wiskott Aldrich syndrome
  • Bare lymphocyte syndrome
  • Ommen syndrome
  • CD40 ligand deficiency
  • IPEX syndrome
  • DOCK8 deficiency
  • Hyper IgE syndrome
  • X-linked lymphoproliferative syndrome
  • Hereditary lympohistocytosis
  • STAT1 gain of function
  • Autoinflamatory syndromes
  • DiGeorge syndrome

Genetic Diseases

  • Adrenoleukodystrophy
  • Mucopolysacchraidosis I (Hurlers Disease)
  • Metachromatic leukodystrophy
  • Gauchers Disease
  • Mucopolysaccharidosis VI (Maroteaux-Lamy)