Pediatric Stem Cell Transplantation Care Team

Maria Grazia Roncarolo, MD, is a professor of stem cell and regenerative medicine, professor of pediatrics and professor of medicine.

Areas of expertise: regulatory T cells to prevent graft-versus-host disease, mechanisms of graft versus leukemia in acute myelogenous leukemia, stem cell gene therapy for genetic diseases, hematopoietic stem cell transplantation for immune dysregulation disorders, immune reconstitution.

Rajni Agarwal, MD, is board certified in pediatrics.

Areas of expertise: hematopoietic stem cell graft manipulation, hematopoietic stem cell transplantation for bone marrow failure syndromes, veno-occlusive disease, infection prevention

Rosa Bacchetta, MD, is a genetic immune disease specialist.

Areas of expertise: genetic autoimmunity, IPEX syndrome, immune dysregulation

Alice Bertaina, MD, PhD, is an associate professor of pediatrics.

Areas of expertise: allogenic stem cell transplantation in children, graft manipulation, immune reconstitution, graft-versus-host disease

Agnieszka Czechowicz, MD, PhD, is an assistant professor of pediatrics.

Areas of expertise: bone marrow failure disorders, Fanconi anemia, stem cell gene therapy for genetic diseases

Tami John, MD, is board certified in pediatric hematology-oncology and pediatrics.

Areas of expertise: stem cell and gene therapies for people with genetic diseases, especially sickle cell disease and thalassemia

Orly Klein, MD, is board certified in pediatric hematology-oncology and pediatrics.

Areas of expertise: immune deficiency, bone marrow failure disorders

Matthew Porteus, MD, PhD, is board certified in pediatric hematology-oncology.

Areas of expertise: gene editing for sickle cell disease, hematopoietic stem cell transplantation for genetic diseases, hematopoietic stem cell biology

Christopher Severyn, MD, is board certified in pediatrics.

Areas of expertise: stem cell transplantation, the influence of the microbiome in stem cell transplant outcomes

Ami Shah, MD, is board certified in pediatric hematology-oncology.

Areas of expertise: late effects and survivorship, metabolic diseases, chronic graft-versus-host disease, pediatric leukemia

David Shyr, MD, is board certified in pediatric hematology-oncology.

Areas of expertise: gene and cell therapy, Wiskott Aldrich syndrome, severe combined immunodeficiency (SCID), leukodystrohies, Hurler syndrome

Katja Weinacht, MD, PhD, is board certified in pediatric hematology-oncology and pediatrics.

Areas of expertise: immune dysregulation, immune-mediated cytopenia, graft-versus-host disease, primary immunodeficiencies, DiGeorge syndrome

Kenneth Weinberg, MD, is board certified in pediatric hematology-oncology and pediatrics.

Areas of expertise: genetic and acquired immune disorders, immune development, hematopoietic stem cell transplantation for genetic diseases, graft-versus-host disease