Gene Therapy Care Teams

Depending on you or your child's diagnosis, your care team may include:

Rosa Bacchetta, MD

Rosa Bacchetta, MD

Dr. Bacchetta is a genetic immune disease specialist. Visit her lab’s website.

Areas of expertise:Gene therapy, immunodysregulation polyendocrinopathy enteropathy x-linked (IPEX) syndrome

Glaivy Batsuli, MD

Glaivy Batsuli, MD

Dr. Batsuli is board certified in Pediatric Hematology-Oncology and Pediatrics. Visit her lab’s website.

Areas of expertise:Hemophilia and other inherited bleeding disorders, thrombotic disorders

Agnieszka Czechowicz, MD, PhD

Agnieszka Czechowicz, MD, PhD

Dr. Czechowicz is an assistant professor of pediatrics. Visit her lab’s website.

Areas of expertise:Gene therapy, stem cell transplantation, Fanconi anemia, non-genotoxic conditioning therapy regimens

Kara Davis, DO

Kara Davis, DO

Dr. Davis is board certified in Pediatric Hematology-Oncology and Pediatrics. Visit her lab’s website.

Areas of expertise:CAR T-cell therapy, high-risk leukemia

Natalia Gomez-Ospina, MD, PhD

Natalia Gomez-Ospina, MD, PhD

Dr. Gomez-Ospina is board certified in Clinical Genetics and Genomics. Visit her lab’s website.

Areas of expertise:Gene therapies for metabolic diseases, including mucopolysaccharidosis type I (MPS I) and Gaucher disease 

Sabine Heitzeneder, PhD

Sabine Heitzeneder, PhD

Dr. Heitzeneder is an assistant professor of pediatrics. Visit her lab’s website.

Areas of expertise:CAR T-cell therapy for childhood cancers, especially brain tumors

Crystal Mackall, MD

Crystal Mackall, MD

Dr. Mackall is the director of the Stanford Center for Cancer Cell Therapy. She is board certified in Pediatric Hematology-Oncology, Pediatrics and Internal Medicine. Visit her lab’s website.

Areas of expertise:CAR T-cell therapy for childhood cancers 

Michelle Monje, MD, PhD

Michelle Monje, MD, PhD

Dr. Monje is board certified in Neurology and Neuro-Oncology. Visit her lab’s website.

Areas of expertise:Neuro-oncology, neuro-immuno-oncology, CAR T-cell therapy

Matthew Porteus, MD, PhD

Matthew Porteus, MD, PhD

Dr. Porteus is a professor of pediatrics and stem cell transplantation. Visit his lab’s website.

Areas of expertise:Gene therapy, stem cell transplantation, sickle cell disease

Sneha Ramakrishna, MD

Sneha Ramakrishna, MD

Dr. Ramakrishna is board certified in Pediatric Hematology-Oncology and Pediatrics. Visit her lab’s website.

Areas of expertise:CAR T-cell therapy for pediatric solid tumors

Maria Grazia Roncarolo, MD

Maria Grazia Roncarolo, MD

Dr. Roncarolo is a professor emerita of pediatrics and stem cell transplantation.

Areas of expertise:Gene therapy, stem cell transplantation, severe combined immunodeficiency (SCID)

Katja Weinacht, MD, PhD

Katja Weinacht, MD, PhD

Dr. Weinacht is board certified in Pediatric Hematology-Oncology and Pediatrics. Visit her lab’s website.

Areas of expertise:Developmental biology of the thymus, development of a therapy using thymic epithelial cells