Gene Therapy Care Teams

Tami John, MD

Dr. John is the Bass Center clinical director of Gene Therapies. She is board certified in Pediatric Hematology-Oncology and Pediatrics.

Areas of expertise:Gene therapy, red blood cell disorders and hemoglobinopathies including sickle cell disease and thalassemia, bone marrow failure disorders, stem cell transplantation, gene therapy clinical research

Ami Shah, MD

Dr. Shah is board certified in Pediatric Hematology-Oncology.

Areas of expertise:Gene therapy, stem cell transplantation, inherited metabolic diseases including adrenoleukodystrophy (ALD) and inherited immune diseases, gene therapy clinical research

Rajni Agarwal, MD

Dr. Agarwal is board certified in Pediatrics.

Areas of expertise:Gene therapy, stem cell transplantation, Fanconi anemia, bone marrow failure disorders, gene therapy clinical research

May Chien, MD

Dr. Chien is board certified in Pediatric Hematology-Oncology, Pediatrics, and Adult Hematology.

Areas of expertise:Hemophilia, sickle cell disease, gene therapy clinical research

Rosa Bacchetta, MD

Dr. Bacchetta is a genetic immune disease specialist.

Areas of expertise:Gene therapy, immunodysregulation polyendocrinopathy enteropathy x-linked (IPEX) syndrome

Agnieszka Czechowicz, MD, PhD

Dr. Czechowicz is an assistant professor of pediatrics.

Areas of expertise:Gene therapy, stem cell transplantation, Fanconi anemia, non-genotoxic conditioning therapy regimens

Matthew Porteus, MD, PhD

Dr. Porteus is a professor of pediatrics and stem cell transplantation.

Areas of expertise:Gene therapy, stem cell transplantation, sickle cell disease

Maria Grazia Roncarolo, MD

Dr. Roncarolo is a professor of pediatrics and stem cell transplantation.

Areas of expertise:Gene therapy, stem cell transplantation, severe combined immunodeficiency (SCID)